Deep brain stimulation before the age of 18 in patients with childhood-onset dyskinetic movement disorders - a German registry for quality assurance

Organizational Data

DRKS-ID:
DRKS00006778
Recruitment Status:
Recruiting ongoing
Date of registration in DRKS:
2014-12-01
Last update in DRKS:
2015-02-13
Registration type:
Retrospective

Acronym/abbreviation of the study

GEPESTIM

URL of the study

No Entry

Brief summary in lay language

Deep brain Stimulation (DBS) has proven to be a safe and effective therapy for primary dystonia. The results in patients with aquired dystonia are variable. So far there is only little data about the effect of deep brain stimulation on movement disorders in paediatric patients. With the the registry all available data of patients with a childhood-onset dyskinetic movement disorder who received DBS before the age of 18 years should be collected. The pre-, peri- and postoperative data encompass medical history of the patients, etiology of disease, evolution of symptoms, pharmacotherapy and supportive therapy, technical details of the DBS implantation, stimulation parameters and complications. The analysis of this data should help to evaluate the effect of DBS comprehensively and to identify possible outcome predictors in order to improve counselling of affected families and to select suitable patients. Furthermore, treatment standards should be created to optimize the service of young patients undergoing DBS.

Brief summary in scientific language

Deep brain Stimulation (DBS) has proven to be a safe and effective therapy for primary dystonia. The results in patients with secondary dystonia are heterogeneous. So far there is only little data about the effect of deep brain stimulation (DBS) on movement disorders in paediatric patients. With the the registry all available data of patients with a childhood-onset dyskinetic movement disorder who received DBS before the age of 18 years should be collected. The pre-, peri- and postoperative data encompass medical history of the patients, etiology of disease, evolution of symptoms, pharmacotherapy and supportive therapy, technical details of the DBS implantation, stimulation parameters and complications. The analysis of this data should help to evaluate the effect of DBS comprehensively and to identify possible outcome predictors in order to improve counselling of affected families and to select suitable patients. Furthermore, treatment standards should be created to optimize the service of young patients undergoing DBS.

Health condition or problem studied

ICD10:
G80.3 - Dyskinetic cerebral palsy
ICD10:
G24.1 - Idiopathic familial dystonia
ICD10:
G23.0 - Hallervorden-Spatz disease
ICD10:
E79.1 - Lesch-Nyhan syndrome
ICD10:
G24.2 - Idiopathic nonfamilial dystonia
Healthy volunteers:
No Entry

Interventions, Observational Groups

Arm 1:
With the aid of the registry data of patients with a childhood-onset dyskinetic movement disorder who received DBS before the age of 18 years should be systematically collected encompassing information on medical history of the patients, disease etiology, evolution of symptoms, pharmacotherapy, supportive therapy, technical details of DBS implantation, stimulation parameters and complications.

Endpoints

Primary outcome:
Change of Burke-Fahn-Marsden Dystonia Rating Scale after Deep Brain Stimulation
Secondary outcome:
Deep Brain Stimulation effect on - dystonia - dyskinesia - pain - memory - affect - quality of life - spasticity - motor function - cognition - attention - speech

Study Design

Purpose:
Treatment
Retrospective/prospective:
No Entry
Study type:
Non-interventional
Longitudinal/cross-sectional:
No Entry
Study type non-interventional:
No Entry

Recruitment

Recruitment Status:
Recruiting ongoing
Reason if recruiting stopped or withdrawn:
No Entry

Recruitment Locations

Recruitment countries:
  • Germany
Number of study centers:
Multicenter study
Recruitment location(s):
  • Medical center Neurologie Düsseldorf
  • Medical center Stereotaxie Hannover
  • Medical center Neurologie Köln
  • Medical center Neurologie Berlin
  • Medical center Pädiatrie Freiburg im Breisgau
  • Medical center Neurologie Kiel

Recruitment period and number of participants

Planned study start date:
No Entry
Actual study start date:
2013-10-14
Planned study completion date:
No Entry
Actual Study Completion Date:
No Entry
Target Sample Size:
60
Final Sample Size:
No Entry

Inclusion Criteria

Sex:
All
Minimum Age:
no minimum age
Maximum Age:
no maximum age
Additional Inclusion Criteria:
- Diagnosis of childhood-onset dyskinetic movement disorders - Deep brain stimulation before the age of 18

Exclusion Criteria

- No diagnosis of childhood-onset dyskinetic movement disorders - Deep brain stimulation after the age of 18

Addresses

Primary Sponsor

Address:
University of Cologne
Albertus-Magnus-Platz
50923 Cologne
Germany
Telephone:
No Entry
Fax:
No Entry
Contact per E-Mail:
Contact per E-Mail
URL:
No Entry
Investigator Sponsored/Initiated Trial (IST/IIT):
Yes

Contact for Scientific Queries

Address:
Uniklinik Köln Neurologie
Univ.-Prof. Lars Timmermann
Kerpenerstr. 62
50937 Köln
Germany
Telephone:
022147887444
Fax:
02214789002
Contact per E-Mail:
Contact per E-Mail
URL:
No Entry

Contact for Public Queries

Address:
Uniklinik Köln Neurologie
Dr. Anne Koy
Kerpenerstr. 62
50937 Köln
Germany
Telephone:
022147887353
Fax:
022147889002
Contact per E-Mail:
Contact per E-Mail
URL:
No Entry

Principal Investigator

Address:
Uniklinik Köln Neurologie
Univ.-Prof. Lars Timmermann
Kerpenerstr. 62
50937 Köln
Germany
Telephone:
022147887444
Fax:
02214789002
Contact per E-Mail:
Contact per E-Mail
URL:
No Entry

Sources of Monetary or Material Support

Institutional budget, no external funding (budget of sponsor/PI)

Address:
Univerität zu Köln
Albertus-Magnus-Platz
50925 Köln
Germany
Telephone:
No Entry
Fax:
No Entry
Contact per E-Mail:
Contact per E-Mail
URL:
No Entry

Ethics Committee

Address Ethics Committee

Address:
Ethikkommission der Medizinischen Fakultät der Universität zu Köln
Gleueler Str. 269
50935 Köln
Germany
Telephone:
+49-221-478 82900
Fax:
+40-221-478 82905
Contact per E-Mail:
Contact per E-Mail
URL:
No Entry

Vote of leading Ethics Committee

Vote of leading Ethics Committee
Date of ethics committee application:
2013-08-07
Ethics committee number:
13-168
Vote of the Ethics Committee:
Approved
Date of the vote:
2013-10-07

Further identification numbers

Other primary registry ID:
No Entry
EudraCT Number:
No Entry
UTN (Universal Trial Number):
No Entry
EUDAMED Number:
No Entry

IPD - Individual Participant Data

Do you plan to make participant-related data (IPD) available to other researchers in an anonymized form?:
No Entry
IPD Sharing Plan:
No Entry

Study protocol and other study documents

Study protocols:
No Entry
Study abstract:
No Entry
Other study documents:
No Entry
Background literature:
No Entry
Related DRKS studies:
No Entry

Publication of study results

Planned publication:
No Entry
Publikationen/Studienergebnisse:
No Entry
Date of first publication of study results:
No Entry
DRKS entry published for the first time with results:
No Entry

Basic reporting

Basic Reporting / Results tables:
No Entry
Brief summary of results:
No Entry